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Mutations in protein coding-sequence and regulatory elements can cause altered gene expression which can cause diseases. Mis-regulated gene expression can be corrected by direct editing of genomic elements. Indeed, artificial transcription factors can regulate gene expression resulting rescue phenotypes. The fact that less than 2% of our genome encodes protein suggests regulatory elements are promising candidates for therapeutics. We aim to identify and develop strategy for correction of disease-associated aberrations using CRISPR and its derivative technology.
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Charles M. Kerr, Sophia E. Silver,Yi Sun Choi,Martha E. Floy,Amy D. Bradshaw,Seung-Woo Cho,Sean P. Palecek,Ying Mei
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Whee-Soo Kim,Sungjin Min,Su Kyeom Kim,Sunghwi Kang,Soohwan An, Ernesto Criado-Hidalgo,Hunter Davis,Avinoam Bar-Zion,Dina Malounda, Yu Heun Kim,Jae-Hyun Lee,Soo Han Bae,
Nature Materialsno. 2 (2024): 290-300
SENSORS AND ACTUATORS B-CHEMICAL (2024): 134884-134884
Sungjin Min,Suran Kim,Woo-Sup Sim,Yi Sun Choi, Hyebin Joo,Jae-Hyun Park, Su-Jin Lee, Hyeok Kim,Mi Jeong Lee, Inhea Jeong, Baofang Cui,Sung-Hyun Jo,
Nature Communicationsno. 1 (2024): 1-22
Jung-Min Oh,Yujin Kang,Jumi Park, Yubin Sung,Dayoung Kim,Yuri Seo,Eun A Lee,Jae Sun Ra,Enkhzul Amarsanaa,Young-Un Park, Seon Young Lee,Jung Me Hwang,
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Bioengineering & Translational Medicineno. 3 (2023): n/a-n/a
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