Modifications in Triglyceride-Rich Lipoprotein Metabolism Induced by Alipogene Tiparvovec (AAV(1)-LPLS447X Gene Therapy) Correlate With Clinical Benefit in Patients with Lipoprotein Lipase Deficiency (LPLD)
Circulation(2010)
关键词
Gene therapy,Lipoproteins,Hyperlipoproteinemia,Clinical trials
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