Phase 1 exploratory efficacy of the novel enzyme replacement therapy neoGAA in treatment-naïve and alglucosidase alfa-treated late-onset Pompe disease patientsLoren Pena,Richard Barohn,Barry Byrne,Claude Desnuelle,Ozlem Goker-Alpan,Shafeeq Ladha,Pascal Laforet,Eugen Mengel,Alan Pestronki,Jean Pouget,Benedikt Schoser,Volker Straub,Jaya Trivedi,Philip Van Damme,John Vissing,Peter Young,Beth Thurberg,Kerry Culm-Merdek,Gerard Short,Ans van der PloegMOLECULAR GENETICS AND METABOLISM（2016）引用 0|浏览44暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
