Correction of both Tay-Sachs and Sandhoff diseases with the PS gene editing systemLi Ou,Michael Przybilla,Alexandru-Flaviu Tăbăran,Paula Overn,Gerard O'Sullivan,Xuntian Jiang,Rohini Sidhu,Pamela Kell,Daniel Ory,Chester B. WhitleyMOLECULAR GENETICS AND METABOLISM(2020)引用 0|浏览20暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要