Lentiviral haematopoietic stem cell gene therapy (HSC-GT) for metachromatic leukodystrophy (MLD): Preliminary results from a clinical trial with a cryopreserved formulation of OTL-200V. Calbi,F. Fumagalli, S. Acquati, S. Miglietta, F. Ciotti, M. Fraschini, M. Sarzana, C. Baldoli, S. Recupero,A. Zambon,F. Barzaghi,F. Ferrua,M. P. Cicalese,M. Migliavacca,F. Tucci,V. Gallo, G. La Marca,P. Silvani,M. Facchini,S. Locatelli,G. Antonioli, S. Zancan, G. Farinelli,F. Morena, J. Segovia, L. C. Schwab,G. Downey, M. Gabaldo,S. Martino, F. Ciceri, M. G. Natali Sora,M. E. Bernardo,L. Naldini,A. AiutiHUMAN GENE THERAPY（2019）引用 0|浏览23暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
