Efficient gene editing of the PKLR locus in human long-term haematopoietic stem cells to correct Pyruvate Kinase Deficiency S. Fananas-Baquero,O. Quintana-Bustamante,O. Alberquilla,R. Sanchez,D. P. Dever,J. Camarena,R. Turk,M. Behlke,J. A. Bueren,M. Porteus,J. C. SegoviaHUMAN GENE THERAPY(2019)引用 0|浏览8暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要