mRNA Therapy for Inherited Disorders of Glycogen Metabolism
Paloma H. Giangrande,Jingsong Cao,Minjung Choi,Eleonora Guadagnin,Marine Silva, Erwann Philippe,Arianna Markel,Jenny Zhuo,Shi Liang,Andrea Frassetto,Lisa Rice,Tatiana Ketova,Cosmin Mihai,David Reid, Maria Abbasi,Anne-Renee Graham,Kristine Burke,Zach Zalinger, Giles Besin,Meredith Wolfrom,Athanasios Dousis,Vladimir Presnyak,Christopher Pepin,Wei Zheng,Lei Ci,Marjie Hard,Edward Miracco,Christine Lukacs,Patrick Finn,Lin Guey, Giles Mithieux,Fabienne Rajas,Paolo Martini MOLECULAR THERAPY(2020)
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