AAV-Mediated Homology-Independent Targeted Integration in Newborn Hepatocytes Corrects Mucopolysaccharidosis Type VIManel Llado Santaeularia,Federica Esposito,Margherita Dell'Anno,Renato Minopoli,Hristiana Lyubenova,Edoardo Nusco,Carolina Iodice, Lucio Di Filippo,Francesco Musacchia,Anna Manfredi,Annalaura Torella,Davide Cacchiarelli,Vincenzo Nigro,Rita Ferla, Alberto AuricchioMOLECULAR THERAPY(2020)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要