Long-Term Rescue of Retinal Degeneration in Rho-P23H Knockin Mice via Dual AAV-Medicated Allele-Specific CRISPR-Cas9 Gene EditingAndrea D'Amico,Rossano Butcher,Benjamin P. Kleinstiver,Nachiket Pendse,Pingjuan Li,Eric Pierce,J. Keith Joung,Qin LiuMOLECULAR THERAPY(2019)引用 0|浏览7暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要