AVXS-101 Gene-Replacement Therapy (GRT) in Spinal Muscular Atrophy Type 1 (SMA1): Long-Term Follow-Up From the Phase 1 Clinical TrialJerry R. Mendell,Kelly J. Lehman,Markus McColly,Linda P. Lowes,Lindsay N. Alfano,Natalie F. Miller,Megan A. Iammarino,Kathleen Church,Francis G. Ogrinc,James L'Italien,Courtney Wells,Douglas M. Sproule,Douglas E. FeltnerNEUROLOGY（2019）引用 13|浏览17暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
