RELATIONS BETWEEN POTENTIATOR RESPONSES IN INTESTINAL ORGANOIDS AND IN VIVO OUTCOME PARAMETERS IN PATIENTS WITH CFTR GATING MUTATIONS

G. Berkers, J. F. Dekkers, E. Kruisselbrink, A. M. Vonk, S. Heida-Michel, M. Geerdink,K. M. de Winter-de Groot, H. G. Arets, I Bronsveld,E. de Graaf, C. J. Majoor,G. H. Koppelman,J. Roukema,H. Janssens,H. Heijerman,R. Vries,H. C. Clevers,H. R. de Jonge,J. Beekman,C. K. van der Ent

PEDIATRIC PULMONOLOGY(2016)

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