Long-term follow-up of the phase 1 start trial of onasemnogene abeparvovec gene therapy in spinal muscular atrophy type 1J. R. Mendell,R. Shell,K. J. Lehman, M. McColly,L. P. Lowes,L. N. Alfano,N. F. Miller,M. A. Iammarino,K. Church, I. Kausar, S. P. Reyna, M. Meriggioli, A. Kleyn,S. Al-ZaidyThorax(2021)引用 1|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要