Impacts and burden of Niemann-Pick disease type C: A patient and caregiver perspectiveEugen Mengel,Marc Patterson,Michael Chladek,Christina Guldberg,Christine I. Dali,Tara Symonds,Lucy Lloyd-Price,Toni Mathieson,Joslyn Crowe,Claire BurbridgeANNALS OF NEUROLOGY(2021)引用 0|浏览6暂无评分关键词Neurometabolic Disorders, Rare DiseasesAI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要