Atherogenic lipid profile in patients with Niemann-Pick disease type B: What treatment strategies?

Journal of Clinical Lipidology(2022)

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摘要
•Atherogenic plasma lipid abnormalities are common in patients with ASMD.•The clinical experiences in lipid-lowering strategies are limited.•Olipudase alfa appears as the most promising candidate for improving lipid profile.
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关键词
Niemann-Pick disease type B,Acid sphingomyelinase deficiency,Lipid abnormalities,Dyslipidemia,Management,Case report,Review
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