A brain penetrant progranulin biotherapeutic rescues lysosomal and inflammatory phenotypes in the brain of
GRN
knockout mice
Todd Logan,Sarah DeVos,Matthew J. Simon,Sonnet Davis,Junhua Wang,Ray Low,Fen Huang,Yashas Rajendra,Rachel Prorok, Elizabeth Sun,Anil Rana,Jennifer Hsiao‐Nakamoto, Sofia Mosesova,Yuda Zhu,Gerald M. Cherf,Bettina Lengerich,Akhil Bhalla,Do Jin Kim,Darren Chan,Joseph Duque,Hai Tran,Melina Lenser,Hoang Nguyen,Roni Chau,Timothy Earr,Mihalis S. Kariolis,Kathryn M. Monroe,Pascal E. Sanchez,Mark S. Dennis,Kirk R. Henne,Kannan Gunasekaran,Giuseppe Astarita,Ryan J. Watts,Zachary K. Sweeney,Joseph W. Lewcock,Ankita Srivastava,Gilbert Di Paolo Alzheimer's & Dementia(2020)
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