ICV Delivery of AAV9-NGLY1 Gene Replacement Therapy Shows Dose Dependent Improvement of Phenotypic and Biomarker Endpoints in Ngly1 Deficient RatsWilliam F. Mueller,Lei Zhu, Jennifer W. Cook,Brandon Tan,Brendan Beahm,Selina Dwight,Matt Wilsey,Brett E. Crawford,Becky SchweighardtMOLECULAR THERAPY(2022)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要