Evaluation of AAV9 Gene Therapy for SMARD1/CMT2S in Different Mouse Models Reveal Differences in Efficacy Dependent on Promoter ChoiceJulieth A. Sierra Delgado, Sarah Holbrook,Shibi Likhite,Vicki McGovern,Monica Nizzardo,Amy N. Hicks, Amy Huffenberger,Shrestha Sinha Ray,Stefania Corti,Arthur Burghes,W. David Arnold,Greg A. Cox,Kathrin C. MeyerMOLECULAR THERAPY(2022)引用 0|浏览10暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要