Onasemnogene abeparvovec (OA) treatment outcomes by patient weight at infusion: Initial findings from the RESTORE registry

L. Servais, K. Benguerba,D. De Vivo,J. Kirschner,E. Mercuri, F. Muntoni, C. Proud, E. Tizzano,S. Quijano-Roy, K. Saito,D. Raju, N. LaMarca, R. Sun, F. Anderson, E. Faulkner,R. Finkel

Neuromuscular Disorders(2022)

引用 0|浏览3
暂无评分
关键词
Neuromuscular Disorders
AI 理解论文
溯源树
样例
生成溯源树,研究论文发展脉络
Chat Paper
正在生成论文摘要