Assessment of Safety and Biodistribution of a miniMECP2 AAV9 Vector for Gene-replacement Therapy of Rett Syndrome in Non-human Primates (NHPs)S. Prasad, G. Flora,M. Newman,S. J. Gray,S. Sinnett,C. SadhuHUMAN GENE THERAPY(2022)引用 0|浏览14暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要