Immunosuppression to Inhibit Capsid-Specific Humoral Immune Responses in High-Dose AAV Gene Therapy in Cynomolgus Macaques

Deniz Erturk-Hasdemir, Weasel Scott, Alexander Kistner, Leah Cardwell, Justin Serio, Lorraine Sullivan, Ruta Phadnis,Brian E. McIntosh,Camille L. Bedrosian,Emil D. Kakkis,Kathleen McKeever,Samuel C. Wadsworth, Reed Clark,Lorelei Stoica,Barbara A. Sullivan

MOLECULAR THERAPY(2023)

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