Long-term safety and efficacy of DTX301 in adults with late-onset ornithine transcarbamylase (OTC) deficiency: A Phase 1/2 trialJanet Thomas,Wen-Hann Tan,Aneal Khan,Laura Konczal, Margo Sheck Breilyn, Leticia Ceberio Hualde, Marie Luz Couce,Tarekegn Geberhiwot,Nathalie Guffon,Cary Harding, Kaushik Patra,J. Lawrence Merritt,Eric CrombezMolecular Genetics and Metabolism（2024）引用 0|浏览2暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
