Phase 1/2 Trial Evaluating AOC 1044 in Healthy Volunteers and Participants with DMD Mutations Amenable to Exon 44 Skipping (DMD44): EXPLORE44 Trial Design (P4-8.007)

Mark Stahl, Elizabeth Ackermann, Yiming Zhu, Yvonne Tami, Steven Hughes, Chamindra Laverty,Craig McDonald

Neurology(2024)

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