Superior outcomes in neuroretina following IV versus intra-CSF AAV9 gene replacement in mice with MPS IIIAKim M. Hemsley,Leanne Winner,Andrew Shoubridge,Emma Parkinson-Lawrence,Adeline Lau, Tabitha-Rose Lance, Barbara King, William Scott,Marten Snel,Paul Trim,Helen BeardMOLECULAR GENETICS AND METABOLISM(2024)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要