Phase 2 open-label extension study (ole) of patisiran, an investigational sIRNA investigational agent for familial amyloid polyneuropathy (fap)
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM(2015)
摘要
Phase 2 open-label extension study (ole) of patisiran, an investigational sIRNA investigational agent for familial amyloid polyneuropathy (fap)
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neurology
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