Evaluator Training and Reliability for SMA Global Nusinersen Trials1.

Journal of neuromuscular diseases(2018)

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摘要
Rigorous evaluator training ensures reliability of assessment of subjects with spinal muscular atrophy (SMA) in multicenter international trials.
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关键词
SMA,multicenter,nusinersen,outcome assessment,outcome measures,reliability of results,spinal muscular atrophy,studies
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