Oral SMN2 splicing modifiers in spinal muscular atrophy: Proof-of-mechanism and ongoing clinical studies Anne Marquet, Stefan Sturm,Heidemarie Kletzl,Andreas Günther,Christian Czech,Agnes Poirier,Timothy Seabrook,Lutz Müller,Russell Kinch,Hasane Ratni,Ksenija Gorni,Friedrich Metzger,Omar KhwajaEuropean Journal of Paediatric Neurology(2017)引用 0|浏览17暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要