Focused ultrasound-induced blood brain-barrier opening enhanced vascular permeability for GDNF delivery in Huntington's disease mouse model.

Brain Stimulation(2019)

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摘要
Schematic representation of FUS-mediated GDNFp-liposomes (GDNFp-LPs) delivery for treatment of HD transgenic mice.Image 1
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关键词
Focused ultrasound,Gene therapy,Blood-brain barrier opening,GDNF,Huntington's disease
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