P.141PPMO-mediated skipping therapy of duplicated exon 2 in the DMD geneL. Gushchina, K. Grounds, H. Huang, E. Frair,F. Schnell, G. Hanson,T. Simmons,N. Wein, K. FlaniganNEUROMUSCULAR DISORDERS(2019)引用 0|浏览6暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要