O.24Biodistribution of onasemnogene abeparvovec (AVXS-101) DNA, mRNA, and SMN protein in human tissue B. Kaspar, G. Thomsen, C. Hsieh,J. Do, S. Solano,B. Chu, B. Barkho,M. Fugere,P. Kaufmann, K. Foust,A. Kaspar, J. L'Italien,D. Sproule, D. Feltner,W. Chung,A. Burghes,V. McGovern,R. Hevner,M. Conces,J. MendellNEUROMUSCULAR DISORDERS(2019)引用 3|浏览17暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要