Editing A Gamma-Globin Repressor Binding Site Restores Fetal Hemoglobin Synthesis And Corrects The Phenotype Of Sickle Cell Disease Erythrocytes
Leslie Weber,Giacomo Frati,Tristan Felix,Clara Wollenschlaeger,Antonio Casini,Vasco Meneghini,Cecile Masson,Anne De Cian,Anne Chalumeau,Fulvio Mavilio,Mario Amendola,Isabelle André,Anna Cereseto,Wassim El Nemer,Jean-Paul Concordet,Carine Giovannangeli,Marina Cavazzana,Annarita Miccio BLOOD(2019)
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