Treatment forms and clinical course of LPS-Responsive beige-like anchor protein deficiency and introduction of the immune deficiency and -dysregulation activity (=IDDA) score Victoria Katharina Tesch , Hassan Abolhassani , Bodo Grimbacher , Arjan Lankaster , Andrew Gennery , Bella Shadur , Polina Stepensky , Yuliya Mareika , Svetlana Sharapova , Elif Karakoc-Aydiner , Jaques G. Riviere , Marina Garcia-Prat , Nicolette Moes , Filomeen Haerynck , Luis I. Gonzales-Granado , Juan Luis Santos Perez , Anna Mukhina , Asghar Aghamohammadi , Lennart Hammarstrom , Figen Dogu , Aydan I. Ikinciogullari , Sevgi Bal , Safa Baris , Sara Sebnem Kilic , Neslihan Edeer Karaca , Necil Kutukculer , Hermann Girschick , Antonios Kolios , Sevgi Keles , Markus G. Seidel BONE MARROW TRANSPLANTATION(2019)
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