ANTISENSE-BASED EXON SKIPPING AS A THERAPY FOR DUCHENNE MUSCULAR DYSTROPHY, STATUS AND PROSPECTS

G. -J. van Ommen, A. Aartsma-Rus,M. Evers,W. van Roon, P. -B. 'tHoen,D. Kemaladewi,S. Verbeek, S. Yllmaz-Elis,H. Dauwerse, S. Lesnik-Oberstein,J. T. den Dunnen,N. Goemans, M. Tulinus,J. Verschuuren,S. de Kimpe, G. Campion,J. van Deutekom

EUROPEAN JOURNAL OF NEUROLOGY(2011)

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