Molecular Evidence of Ex Vivo Gene Editing in a Mouse Model of Immunodeficiency
Hayder H. Abdul-Razak,Celine Rocca,Steve J. Howe, Maria Eugenia Alonso-Ferrero,Jianbin Wang,Richard Gabriel,Cynthia Bartholomae,C. H. Victor Gan,Marina I. Garin,Alison Roberts,Michael P. Blundell,Versha Prakash,Francisco Javier Molina-Estevez, Julia Pantoglou, Guillermo Gueenechea,Michael C. Holmes,Philip D. Gregory,Christine Kinnon,Christof von Kalle,Manfred Schmidt,Juan A. Bueren,Adrian J. Thrasher,Rafael J. Yanez-Munoz MOLECULAR THERAPY(2017)
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