AAV.CAPN3 gene therapy for Limb-girdle muscular dystrophy type 2A (LGMD2A): Phenotypic improvements in the calpain3 (CAPN3)-null mouseB. Ozes, D. Murrey,M. Myers,L. Chen, K. Moss, A. Ridgley, C. Wier,Z. SahenkNEUROMUSCULAR DISORDERS(2020)引用 0|浏览2暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要