AAV.CAPN3 gene therapy for Limb-girdle muscular dystrophy type 2A (LGMD2A): Phenotypic improvements in the calpain3 (CAPN3)-null mouse

B. Ozes, D. Murrey,M. Myers,L. Chen, K. Moss, A. Ridgley, C. Wier,Z. Sahenk

NEUROMUSCULAR DISORDERS(2020)

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