Long-Term Outcomes After Gene Therapy For Adenosine Deaminase Severe Combined Immune Deficiency (Ada Scid)
Donald Koh,Omar Habib, Bryanna Reinhardt,Kit Shaw,Elizabeth Garabedian,Dayna Terrazas,Beatriz Campo Fernandez,Satiro De Oliveira,Theodore Moore,Alan Ikeda,Barbara Engel,Gregory Podsakoff,Roger Hollis,Augustine Fernandes, Connie Jackson,Sally Shupien,Suparna Mishra,Alejandra Davila,Jack Mottahedeh,Andrej Vitomirov, John Everett, Aoife Roche,Pascha Hokama,Shantan Reddy,Xiaoyan Wang,Kenneth Cornetta,Michael Hershfield,Robert Sokolic,Harry Malech,Frederick Bushman,Fabio Candotti JOURNAL OF CLINICAL IMMUNOLOGY(2021)
关键词
ADA SCID, Gene Therapy, Long-term Follow-up, Gamma-retroviral vector
AI 理解论文
溯源树
样例