A Phase 2 Clinical Trial Evaluating The Safety And Efficacy Of Srp-9001 For Treating Patients With Duchenne Muscular DystrophyJ. Mendell,P. Shieh,Z. Sahenk,K. Lehman,L. Lowes,N. Reash,M. Iammarino,L. Alfano,B. Powers,J. Woods,C. Skura,H. Mao,L. Staudt,R. Potter,D. Griffin,S. Lewis,L. Hu,S. Upadhyay,T. Singh,L. Rodino-KlapacNEUROMUSCULAR DISORDERS(2021)引用 0|浏览7暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要