Who should be eligible for gene therapy clinical trials in red blood cell pyruvate kinase deficiency (PKD)?: Toward an expanded definition of severe PKD

AMERICAN JOURNAL OF HEMATOLOGY(2022)

引用 3|浏览20
暂无评分
关键词
Gene Therapy,QOL,chronic hemolytic anemia,pyruvate kinase deficiency,splenectomy
AI 理解论文
溯源树
样例
生成溯源树,研究论文发展脉络
Chat Paper
正在生成论文摘要