Multicenter AAV Gene Therapy Studies for SMARD1/CMT2S Establish Safety and Efficacy in Multiple Animal Models and Pave the Way for Initiation of a Phase I/II Clinical TrialJulieth A. Sierra Delgado,Shibi Likhite,Sarah E. Holbrook,Vicki McGovern, Deepti Chung,Joseph Caporale,XIaojin Zhang,Maura Schwartz,Megan Baird, Chase Haubert,Abuzar Kaleem,Annalisa Hartlaub,Natalie Rohan, Erin Ratzlaff,Chris Pierson,Brad Bolon,Pablo Morales,W. David Arnold,Arthur Burghes,Greg A. Cox,Kathrin C. MeyerMOLECULAR THERAPY（2022）引用 0|浏览11暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
