P.124 EDG-5506 targets fast skeletal myosin and reduces muscle damage biomarkers in a phase 1 trial in Becker muscular dystrophy (BMD)

J. Donovan, N. Kilburn, G. Gordon,B. Barthel,M. DuVall, A. Bronson,A. Russell, C. Sherman, M. Evanchik

Neuromuscular Disorders(2022)

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