Second Generation Adeno-Associated Viral Vector Using a Novel Factor VIII Variant with Improved Secretion Achieves Higher Factor VIII Expression in Non-Human Primates

Giang N. Nguyen,Maria C. Seleme, Jonathan R. Lindgren, Allysen C. Henriksen,Amy Muehlmatt, Melanie McFadden,Geary R. Smith,Denise E. Sabatino

Blood(2022)

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