Ataluren Preserves Upper Limb Function in nmDMD Patients from Study 041, a Phase 3 Placebo-Controlled Trial, and the STRIDE Registry
Craig M. McDonald,Eugenio Mercuri,Francesco Muntoni,Heather Gordish-Dressman,Lauren P. Morgenroth,Maria Bernadete Dutra De Resende,Shuizhen Zhou,Mathukumalli Lakshmi Neeharika,Kazuhiro Haginoya,Leigh Ramos-Platt, Paula Williams,Vinay Penematsa,Connie Chou,Min Lin,Shelley Johnson,Karyn Koladicz, Nicholas Mastrandrea,Christian Werner,Panayiota Trifillis NEUROMUSCULAR DISORDERS(2023)
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