CL002, An AAV9 vector expressing engineered miRNA targeting knockdown of GluK2-containing kainate receptors as a novel gene therapy approach for treating intractable temporal lobe epilepsy C. Boileau, S. Deforges,A. Giles, A. Peret, D. Scavarda, F. Bartholomei, N. Partouche, J. Gautron, J. Viotti, G. Penchet, C. Marchal, A. Trebuchon, N. Villeneuve, J. Rumi,T. Marissal,R. Khazipov,I. Khalilov, A. Lepine, M. Milh, D. Figarella-Branger, E. Dougy, S. Tong,R. Appay,A. Mercer, J. Smith, O. Danos, R. H. Porter, C. Mulle, V. CrepelHUMAN GENE THERAPY(2021)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要