DUX4 Optimization for the Development of an Antibodyoligonueleoti.de Conjugate (AOC) for the Treatment of FSHD

Barbora Malecova,David Sala, Garineh Mary Melikian, Gulin Erdogan, Rachel Johns, Joanne Young, Erwann Ventre,Sole Gatto, Matthew Onorato,Adam Pavlicek, Orsolya Kiraly,Martin Koegler,Arthur A. Levin,Philipp Hadwiger, Mike Flanagan,Mark Stahl

NEUROLOGY(2022)

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