Analyzing gene editing enhancers and hematopoietic stem and Progenitor cell clonality using DNA barcoding for the treatment of Pyruvate Kinase Deficiency

I. Ojeda-Perez,A. Bustos, S. Fananas-Baquero, M. Dessy-Rodriguez, V. Lang,O. Alberquilla, A. Garcia-Torralba, R. Torres-Ruiz,S. Rodriguez-Perales, R. Sanchez-Dominguez, C. Trigueros,R. Mayo-Garcia, O. Quintana-Bustamante,J. C. Segovia

HUMAN GENE THERAPY(2022)

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