Modelling Machado-Joseph Disease in patientderived isogenic lines by CRISPR/Cas9-mediated correction of ATXN3-CAG expansionP. Perdigao,C. Matos,S. Lopes, R. Fernandes,M. Lopes, A. Conceicao, R. Faro,M. Santana, D. Adao,D. Rufino-Ramos,K. Leandro,R. Nobre,L. Pereira de AlmeidaHUMAN GENE THERAPY(2022)引用 0|浏览8暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要