Pre-clinical development of an ex-vivo Hematopoietic Stem/progenitor Cells-gene therapy for a-Mannosidosis P. Quaranta, A. A. Rilievo, L. Basso-Ricci,R. J. Hernandez, C. Forni, I. Visigalli, P. Albertini, A. Paoli,A. Morrone,R. Parini, B. Gentner, S. Crippa,M. E. Bernardo,S. Scala,A. AiutiHUMAN GENE THERAPY(2022)引用 0|浏览7暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要