DosEmi study protocol: a phase IV, multicentre, open-label, crossover study to evaluate non-inferiority of pharmacokinetic-guided reduced dosing compared with conventional dosing of emicizumab in people with haemophilia A.

BMJ open(2023)

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摘要
V.4.1 on 28 October 2022 (DosEmi protocol_V4.1; NL81112.041.22).
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关键词
bleeding disorders & coagulopathies, epidemiologic studies, paediatrics, clinical pharmacology, clinical trials
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