Gene Editing/Gene Therapies: NON-VIRAL DNA DELIVERY ASSOCIATED TO TALEN® GENE EDITING LEADS TO HIGHLY EFFICIENT CORRECTION OF SICKLE CELL MUTATION IN LONG-TERM REPOPULATING HEMATOPOIETIC STEM CELLS
Cytotherapy(2023)
关键词
sickle cell mutation,gene therapies,stem cells,non-viral,long-term
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