Preliminary Assessment of the Phase 1/2 Clinical Trial Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of AOC 1001 Administered Intravenously to Adult Patients with Myotonic Dystrophy Type 1 (DM1) (MARINA)

Nicholas Johnson,John Day,Johanna Hamel,Charles Thornton, S. Subramony,Payam Soltanzadeh,Jeffrey Statland,William Arnold,Matthew Wicklund, Kelly Ditrapani, Carrie Heusner, Chao-Yin Chen, Bradley McEvoy, Yiming Zhu,Li-Jung Tai, Elizabeth Ackermann

NEUROLOGY(2023)

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