ICV Administered AAV9-NGLY1 Gene Replacement Therapy (GS-100) Improves Motor Function and Biomarker Outcomes in Ngly1 Deficient RatsLei Zhu,William F. Mueller, Jennifer W. Cook,Brandon Tan,Alicia Newton,Selina S. Dwight,Brendan Beahm,Matt Wilsey,Brett E. Crawford, Becky SchweighardtMOLECULAR THERAPY(2023)引用 0|浏览3暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要